Long-term CBD for Lennox-Gastaut: 48-60% Seizure Reduction Sustained

What Researchers Found About Epilepsy and Cannabis

Updated January 25, 2026Epilepsia, 2019

The Study at a Glance

Positive Results

Published

Epilepsia, 2019

Researchers

Multiple institutions (International)

Study Type

Observational Study

Participants

366 patients · Median 38 weeks

Key Finding

Long-term add-on CBD treatment had an acceptable safety profile in patients with LGS and led to sustained reductions in seizures.

Key Finding: Long-term add-on CBD treatment had an acceptable safety profile in patients with LGS and led to sustained reductions in seizures.

What Researchers Studied About Epilepsy and Cannabis

Patients with Lennox-Gastaut syndrome (LGS) who completed one of two randomized controlled trials (GWPCARE3 or GWPCARE4) were invited to enroll in an open-label extension study.

This study evaluated long-term safety and efficacy of pharmaceutical CBD (Epidiolex).

Of 368 patients who completed the original RCTs, 366 (99.5%) enrolled in this extension.

How This Observational Study Was Conducted

Patients received pharmaceutical CBD oral solution (Epidiolex; 100 mg/mL), titrated from 2.5 to 20 mg/kg/day over a 2-week titration period, added to their existing medications.

Doses could be reduced if not tolerated or increased up to 30 mg/kg/day if beneficial.

Median treatment duration was 38 weeks at a mean modal dose of 23 mg/kg/day. This interim analysis was based on a November 2016 data cut.

Epilepsy Treatment Results

The Main Results:

  • 1366 patients enrolled (99.5% of those completing original RCTs)
  • 2Median treatment duration: 38 weeks at mean dose of 23 mg/kg/day
  • 3Drop seizures: 48-60% median reduction from baseline through week 48
  • 4Total seizures: 48-57% median reduction from baseline through week 48
  • 588% of patients/caregivers reported improvement on Global Impression of Change
  • 6Adverse events in 92.1% of patients (mild 32.5%, moderate 43.4%)
  • 7Common AEs: diarrhea (26.8%), somnolence (23.5%), convulsion (21.3%)
  • 89.6% (35 patients) discontinued due to adverse events
  • 9Liver transaminase elevations in 10.1% (37 patients), 29 on valproic acid

By the Numbers

StatisticWhat It Means
366 patientsLGS patients enrolled in long-term extension (99.5% of eligible)
48-60%Median reduction in drop seizures sustained through 48 weeks
88%Patients/caregivers reporting improvement on Global Impression scale
10.1%Patients with liver transaminase elevations (mostly on valproic acid)
366 patients

LGS patients enrolled in long-term extension (99.5% of eligible)

48-60%

Median reduction in drop seizures sustained through 48 weeks

88%

Patients/caregivers reporting improvement on Global Impression scale

10.1%

Patients with liver transaminase elevations (mostly on valproic acid)

What This Means for Epilepsy Patients

This study provides important long-term data on CBD for Lennox-Gastaut syndrome, one of the most severe forms of childhood epilepsy.

Nearly all patients (99.5%) who completed the original trials chose to continue CBD, suggesting they found it beneficial. Over a median of 38 weeks, CBD maintained substantial seizure reductions: drop seizures decreased by 48-60% and total seizures by 48-57%.

Perhaps most meaningfully, 88% of patients or caregivers reported improvement in overall condition.

While adverse events were common (92.1%), most were mild to moderate. The main concern is liver enzyme elevations in 10.1% of patients, particularly those also taking valproic acid, though most cases resolved with dose adjustments.

For families dealing with LGS, this confirms CBD can provide sustained benefit over the long term.

Quick Answers: Epilepsy and Cannabis

Direct answers based on the findings of this study:

Research Summary: Answers are based on published peer-reviewed studies and represent research findings, not medical recommendations. Individual results may vary. Always consult a healthcare provider before making treatment decisions.

How long can you take CBD for Lennox-Gastaut syndrome?

Yes, CBD can be taken safely long-term. 366 LGS patients took CBD for a median of 38 weeks with sustained seizure reduction (48-60% for drop seizures) and acceptable safety.

Source: Thiele et al., Epilepsia, 2019 (PMID: 30740695)

Does CBD keep working for LGS seizures over time?

Yes. In a 366-patient extension study, CBD maintained its effect through 48 weeks: drop seizures reduced 48-60%, total seizures reduced 48-57%. 88% of patients/caregivers reported continued improvement.

Source: Thiele et al., Epilepsia, 2019 (PMID: 30740695)

What monitoring is needed for long-term CBD in LGS?

Liver function monitoring is essential, especially with valproic acid (10.1% had elevated enzymes, mostly on valproate). Common long-term side effects include diarrhea (26.8%), sleepiness (23.5%), and seizures (21.3%). 9.6% discontinued due to adverse events.

Source: Thiele et al., Epilepsia, 2019 (PMID: 30740695)

This is educational content, not medical advice

The research summarized here is for informational purposes only. Individual results may vary, and what works in studies may not work the same way for everyone. Always consult with a qualified healthcare provider before making changes to your treatment plan or starting medical cannabis therapy.

Important Limitations

This study has some caveats to keep in mind when interpreting the results:

  • Open-label design (no placebo comparison in extension)
  • Adverse events in 92.1% of patients
  • 9.6% discontinued due to adverse events
  • Liver monitoring required, especially with valproic acid
  • Cannot separate CBD effect from natural disease fluctuation

The Bottom Line on Cannabis for Epilepsy

This open-label extension of 366 LGS patients shows CBD benefits are sustained long-term. Over 38 weeks median treatment, drop seizures decreased 48-60% and total seizures 48-57%. 88% reported improvement. Adverse events were common (92.1%) but mostly mild/moderate. Liver monitoring is essential, especially with valproic acid (10.1% had elevations). This confirms CBD as a viable long-term option for LGS.

Do You Qualify for Medical Marijuana?

If you're living with Epilepsy, you may qualify for a medical marijuana card. Our licensed physicians can evaluate you from home via telehealth.

Related Research & Resources

Source

Thiele E, Marsh E, Mazurkiewicz-Beldzinska M, et al. "Cannabidiol in patients with Lennox-Gastaut syndrome: Interim analysis of an open-label extension study" Epilepsia. 2019. DOI: 10.1111/epi.14670

Study information sourced from PubMed®, U.S. National Library of Medicine.

Medically Reviewed By

MMJ.com Medical Advisory Board

Last Updated: January 25, 2026

Important Information

Study Age: This study was published 7 years ago. Newer research may have updated or refined these findings.

Not Medical Advice: This research summary is for educational purposes only. It should not be used to diagnose, treat, cure, or prevent any disease or medical condition. Always consult a qualified healthcare provider before starting or changing any treatment.

Individual Variation: Research findings represent group averages. Your individual response to cannabis may differ based on genetics, other medications, underlying conditions, and many other factors.

Last reviewed: January 25, 2026

Important Notices

Research Summary Disclaimer

This content represents our interpretation of published scientific research for educational purposes. It should not be used to make treatment decisions without consulting a qualified healthcare provider. Individual results may vary from study findings.

FDA Notice

These statements have not been evaluated by the FDA. Cannabis is not intended to diagnose, treat, cure, or prevent any disease. The FDA has not approved cannabis for any medical condition except specific prescription medications.

Copyright & Fair Use

Research summaries are provided under fair use (17 U.S.C. § 107) for educational purposes. We provide brief summaries with attribution, not full reproductions. All studies remain the intellectual property of their respective authors and publishers.

Data Sources

Study information sourced from PubMed®, U.S. National Library of Medicine. Inclusion does not imply endorsement by NLM, NIH, or the federal government.

For complete information, see our Terms of Use and Research Content Policy.

FAQs: Cannabis for Epilepsy

Does CBD work long-term for Lennox-Gastaut syndrome?

Yes. In this extension study of 366 patients, CBD maintained its seizure-reducing effect over a median of 38 weeks. Drop seizures were reduced 48-60% and total seizures 48-57%. 88% of patients/caregivers reported improvement.

What are the long-term side effects of CBD for LGS?

Adverse events occurred in 92.1% of patients but were mostly mild (32.5%) or moderate (43.4%). Common side effects were diarrhea (26.8%), sleepiness (23.5%), and seizures (21.3%). 9.6% discontinued due to adverse events.

Is CBD safe with valproic acid for epilepsy?

Caution is needed. In this study, 10.1% of patients had liver enzyme elevations, and 29 of 37 affected patients were taking valproic acid. Most cases resolved with dose adjustments. Regular liver monitoring is recommended.